Commission publishes joint clinical assessment report on an advanced therapy medicine for spinal muscular atrophy
07 September 2026 by Wendy WINN (DG SANTE, European Commission)The Commission has just published a joint clinical assessment (JCA) report: on onasemnogene abeparvovec (Itvisma), an advanced therapy medicinal product for the treatment of spinal muscular atrophy (SMA). The assessments were carried out by competent authorities of Ireland and France under the EU...